D. Schwartz and J. Lellouch, Explanatory and pragmatic attitudes in therapeutical trials, J Chronic Dis, vol.20, issue.8, pp.637-685, 1967.

K. Claxton, The irrelevance of inference: a decision-making approach to the stochastic evaluation of health care technologies, J Health Econ, vol.18, issue.3, pp.341-64, 1999.

A. A. Stinnett and J. Mullahy, Net health benefits: a new framework for the analysis of uncertainty in cost-effectiveness analysis, Med Decis Making, vol.18, issue.2, pp.68-80, 1998.

H. Raiffa and R. Schlaifer, Applied Statistical Decision theory, 1961.

S. D. Ramsey, R. J. Willke, H. Glick, S. D. Reed, F. Augustovski et al., Cost-effectiveness analysis alongside clinical trials II-an ISPOR good research practices task force report, Value Health, vol.18, issue.2, pp.161-72, 2015.

S. Petrou and A. Gray, Economic evaluation alongside randomised controlled trials: design, conduct, analysis, and reporting, Clinical research, vol.342, 1548.

S. Piantadosi, Clinical trials: a methodologic perspective, 2005.

C. L. Meinert, Clinical Trials: Design, conduct and analysis, 2012.

A. H. Briggs and A. M. Gray, Power and sample size calculations for stochastic costeffectiveness analysis, Med Decis Making, vol.18, issue.2, pp.81-92, 1998.

H. A. Glick, Sample size and power for cost-effectiveness analysis (part 1), PharmacoEconomics, vol.29, issue.3, pp.189-98, 2011.

M. J. Al, B. A. Van-hout, B. C. Michel, and F. F. Rutten, Sample size calculation in economic evaluations, Health Econ, vol.7, issue.4, pp.327-362, 1998.

A. R. Willan and E. M. Pinto, The value of information and optimal clinical trial design, Stat Med, vol.24, issue.12, pp.1791-806, 2005.

A. R. Willan and D. Y. Lin, Incremental net benefit in randomized clinical trials, Stat Med, vol.20, issue.11, pp.1563-74, 2001.

A. R. Willan, Incremental net benefit in the analysis of economic data from clinical trials, with application to the CADET-Hp trial, Eur J Gastroenterol Hepatol, vol.16, issue.6, pp.543-552, 2004.

A. Gray, P. Clarke, J. Wolstenholme, and S. Wordsworth, Applied methods of costeffeciveness analysis in health care, 2011.

Z. Philips, K. Claxton, and S. Palmer, The half-life of truth: what are appropriate time horizons for research decisions?, Med Decis Making, vol.28, issue.3, pp.287-99, 2008.

S. C. Chow, H. Wang, and J. Shao, Sample size calculations in clinical research, 2008.

, Choix méthodologiques pour l'évaluation économique à la HAS, 2011.

R. C. Griggs, M. Batshaw, M. Dunkle, R. Gopal-srivastava, K. E. Krischer et al., Clinical research for rare disease: opportunities, challenges, and solutions, Mol Genet Metab, vol.96, issue.1, pp.20-26, 2009.

S. G. Thompson and R. M. Nixon, How sensitive are cost-effectiveness analyses to choice of parametric distributions?, Med Decis Making, vol.25, issue.4, pp.416-439, 2005.

S. Eckermann and A. R. Willan, Time and expected value of sample information wait for no patient, Value Health, vol.11, issue.3, pp.522-528, 2008.