Gene Therapy in a Patient with Sickle Cell Disease

Jean-Antoine Ribeil 1, 2 Salima Hacein-Bey-Abina 3, 4 Emmanuel Payen 5, 6 Alessandra Magnani 1, 2 Michaela Semeraro 5, 7, 8 Elisa Magrin 1, 2 Laure Caccavelli 1, 2 Bénédicte Neven 9, 5, 7 Philippe Bourget 10 Wassim El Nemer 11, 12 Pablo Bartolucci 13, 14, 15 Leslie Weber 2, 5, 7 Herve Puy 15, 16 Jean-François Meritet 17 David Grévent 10 Yves Beuzard 6 Stany Chretien 5, 6 Thibaud Lefebvre 16, 15 Robert Ross 18 Olivier Negre 5, 18 Gabor Veres 18 Laura Sandler 18 Sandeep Soni 18 Mariane de Montalembert 19 Stéphane Blanche 9 Philippe Leboulch 5, 6, 20, 21, * Marina Cavazzana 1, 2, 5, 7, *
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Jean-Antoine Ribeil, Salima Hacein-Bey-Abina, Emmanuel Payen, Alessandra Magnani, Michaela Semeraro, et al.. Gene Therapy in a Patient with Sickle Cell Disease. New England Journal of Medicine, Massachusetts Medical Society, 2017, 376 (9), pp.848 - 855. ⟨10.1056/NEJMoa1609677⟩. ⟨inserm-01834781⟩

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