Anna Buj-Bello, Françoise Fougerousse, Yannick Schwab, Nadia Messaddeq, Danièle Spehner, et al.. AAV-mediated intramuscular delivery of myotubularin corrects the myotubular myopathy phenotype in targeted murine muscle and suggests a function in plasma membrane homeostasis..
Human Molecular Genetics, Oxford University Press (OUP), 2008, 17 (14), pp.2132-43.
⟨10.1093/hmg/ddn112⟩.
⟨inserm-00311078⟩